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Diseases
Genes (616)
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ABHD5
Cerebral Creatine Deficiency
GAMT
Guanidinoacetate Methyltransferase Deficiency
MYO5B
Microvillus Inclusion Disease
FMR1
Fragile X-Associated Tremor/ataxia Syndrome
Fg Syndrome
CPT1A
Carnitine Palmitoyltransferase I Deficiency
SLC17A5
Salla Disease
MED12
Fg Syndrome
ALS2
Infantile-Onset Ascending Hereditary Spastic Paralysis
UMOD
Medullary Cystic Kidney Disease
NGLY1
Ngly1 Deficiency
MC2R
Familial Glucocorticoid Deficiency
IFIH1
Singleton Merten Syndrome
DMPK
Myotonic Dystrophy
STX3
Microvillus Inclusion Disease
SRD5A2
Alopecia, Androgenetic, 1
AR
Alopecia, Androgenetic, 1
CNBP
Myotonic Dystrophy
RB1
Pinealoblastoma
Trilateral Retinoblastoma
WWTR1
Epithelioid Hemangioendothelioma
CAMTA1
Epithelioid Hemangioendothelioma