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Diseases
Genes (568)
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ABHD5
Cerebral Creatine Deficiency
SLC6A19
Hartnup Disease
GAMT
Guanidinoacetate Methyltransferase Deficiency
TTPA
Familial Isolated Vitamin E Deficiency
ATRX
Alpha-Thalassemia Mental Retardation Syndrome
CPT1A
Carnitine Palmitoyltransferase I Deficiency
PMM2
Pmm2 Deficiency
TMC6
Epidermodysplasia Verruciformis
IDH1
Ollier Disease
Alpha-Thalassemia Mental Retardation Syndrome
PQBP1
Renpenning's Syndrome
TAF1
Dystonia 3, Torsion, X-Linked
UMOD
Medullary Cystic Kidney Disease
FAM20A
Enamel-Renal Syndrome
IFIH1
Singleton Merten Syndrome
NOTCH3
Cadasil
IDH2
Ollier Disease
Alpha-Thalassemia Mental Retardation Syndrome
TMC8
Epidermodysplasia Verruciformis
ASS1
Citrullinemia Type I
SLC4A4
Proximal Renal Tubular Acidosis
STXBP2
Hemophagocytic Lymphohistiocytosis, Familial, 3