Glycogen Storage Disease Due To Acid Maltase Deficiency, Late-Onset

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Retrieved
2021-01-23
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Glycogen storage disease due to acid maltase deficiency, late onset (AMDL), a form of Glycogen storage disease due to acid maltase deficiency (AMD), a degenerative metabolic myopathy particularly affecting respiratory and skeletal muscles, is characterized by an accumulation of glycogen in lysosomes.